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CAMBRIDGE, Mass., May 12, 2026 (GLOBE NEWSWIRE) -- Agios Pharmaceuticals, Inc. (Nasdaq: AGIO), a commercial-stage biopharmaceutical company focused on delivering…

Sickle cell disease (SCD) is one of the most prevalent autosomal recessive conditions worldwide, affecting more than 600,000 newborns annually. Despite advances in…

HLA-matched sibling donor (MSD) hematopoietic cell transplantation (HCT) done prior to adolescence demonstrated promising safety and efficacy outcomes among…

In the tribal communities of Odisha and the plains of Gujarat, a disease has traveled quietly through bloodlines for centuries, unannounced and largely unaddressed…

Doctors with Disabilities has urged J P Nadda to restore thalassemia and sickle cell screening in RBSK 2.0. They say the exclusion weakens early diagnosis and…

AbstractBackground: People with sickle cell disease (SCD) are at risk for accelerated biological aging and functional decline due to both age and SCD-related…

Key PointsQuestion  Do hydroxyurea use (ie, taking the medication at all) and adherence (ie, days taken per week) change over time, and are they associated…

ObjectivesTo determine whether adults with sickle cell disease (SCD) without glaucoma exhibit subclinical structural optic neuropathy (SON) on optical coherence…

Casgevy’s approval changed the sickle cell disease landscape. Developed by Vertex Pharmaceuticals and CRISPR Therapeutics, the therapy showed that the…

A reduced-intensity bone marrow transplant regimen developed by Johns Hopkins physicians provides durable engraftment with low rejection rates and also may preserve…