Phase 1/2 Study to Evaluate the Safety, Tolerability and Pharmacokinetics of HQK-1001 Administered Daily in Patients With Sickle Cell Disease

Clinical Trial
Study Details
Enrollment
24
Interventions
Description

Matching placebo capsule. Administered orally once a day on dosing days.

Name
Placebo
Type
Drug
Description

HQK-1001 capsules. 10 mg/kg, 20 mg/kg or 30 mg/kg administered once a day on dosing days.

Name
HQK-1001
Type
Drug
Phase
Phase 1
Phase 2
Status
COMPLETED
Study ID #
NCT00842088
Study Type
Interventional
Summary

The purpose of this study is to assess the safety and tolerability of HQK-1001 administered for a total of 12 weeks (with one dosing break) in subjects with sickle cell disease.

Study Overview
Conditions
Contacts and Locations
Locations
Facility

Trialogic Research
Madison, Alabama 35758
United States

GeoPoint
34.69926, -86.74833
Facility

Children's Hospital and Research Center at Oakland
Oakland, California 94609
United States

GeoPoint
37.80437, -122.2708
Facility

Century Clinical Research, Inc.
Daytona Beach, Florida 32117
United States

GeoPoint
29.21081, -81.02283
Facility

Medical College of Georgia
Augusta, Georgia 30912
United States

GeoPoint
33.47097, -81.97484
Facility

University of Illinois at Chicago
Chicago, Illinois 60612
United States

GeoPoint
41.85003, -87.65005
Facility

Johns Hopkins School of Medicine
Baltimore, Maryland 21205
United States

GeoPoint
39.29038, -76.61219
Facility

UNC Comprehensive Sickle Cell Program
Chapel Hill, North Carolina 27599
United States

GeoPoint
35.9132, -79.05584
Facility

Texas Children's Cancer Center and Hematology Service
Houston, Texas 77030
United States

GeoPoint
29.76328, -95.36327
Facility

University of the West Indies, Mona
Kingston
Mona
Jamaica

GeoPoint
17.99702, -76.79358